Designing and generating a mouse model: frequently asked questionsChannabasavaiah B.Gurumurthy,Thomas L.Saunders,Masato Ohtsuka76-90
Harnessing CRISPR-Cas system diversity for gene editing technologiesAlexander McKay,Gaetan Burgio91-106
Therapeutic gene editing strategies using CRISPR-Cas9 for the β-hemoglobinopathiesJames B.Papizan,Shaina N.Porter,Akshay Sharma,Shondra M.Pruett-Miller115-134
Genome engineering technologies in rabbitsJun Song,Jifeng Zhang,Jie Xu,Minerva Garcia-Barrio,Y.Eugene Chen,Dongshan Yang135-147
Progress and challenges in CRISPR-mediated therapeutic genome editing for monogenic diseasesColin T.Konishi,Chengzu Long148-162
A transgenic pig model expressing a CMV-ZsGreen1 reporter across an extensive array of tissuesAmy T.Desaulniers,Rebecca A.Cederberg,Elizabeth P.Carreiro,Channabasavaiah B.Gurumurthy,Brett R.White163-173
Generating a CRISPR knockout mouse through a strong premature termination codon: a cautionary taleQing Rex Lyu,Peng Yao,Joseph M.Miano174-178